Here you will find summaries of the progress in research to treat Usher syndrome. Research is organized by gene-specific treatment approaches and research progress for all subtypes of Usher syndrome, as well as gene-independent (also known as gene agnostic) approaches that have the potential to benefit anyone with USH (i.e. stem cell therapy, neuroprotection, optogenetics, etc.)

To review the basics of Usher syndrome and the three clinical types, click here.

The National Institute of Health's Glossary of Common Terms can help you learn about terminology related to clinical trials.

The National Institute of General Medical Sciences has a glossary of terms related to biomedical research.



Gene-Specific Approaches:

You are not alone.

Join the USH Trust to be informed of clinical trials and the latest advances in research. 

Join the USH Blue Book to connect with individuals with Usher syndrome, family members and friends in a global network of support.

Locate experts in the USH Yellow Book, a centralized directory of researchers and resources worldwide.