To design strong clinical trials, scientists need to understand how a disease changes over time and how to measure treatment effects. In this study, researchers at 16 sites in Europe and North America used simple, non-invasive tests to study the eye health of 105 people with USH2A. Their findings helped show how USH2A-related conditions progress and which vision tests work best, leading to recommendations for designing better future clinical trials.
To design a good clinical trial, scientists need to understand how a disease changes over time and how to measure whether a treatment is working.
